Dr. Natalia Gomez Ospina

Biography

Dr. Natalia Gomez-Ospina leads a research lab focused on the development of precise genetic medicines using genome editing techniques. The lab primarily targets childhood neurodegenerative diseases and lysosomal storage disorders through the use of genome-edited stem cells for definitive treatments. Current projects include developing autologous transplantation strategies using genome-edited hematopoietic stem cells for conditions such as Mucopolysaccharidosis type I, Gaucher's disease, Krabbe disease, Frontotemporal Dementia, and Friedreich's ataxia. The lab emphasizes a strong translational focus, investigating both the basic science questions that underpin these diseases and the efficiency of genome editing tools. Dr. Gomez-Ospina's training includes a dual MD/Ph.D. from Stanford Medical School, where her doctoral research concentrated on voltage-gated calcium channels. She completed her residency in Medical Genetics after initial training in internal medicine and dermatology. As a board-certified Medical Geneticist, her clinical responsibilities involve evaluating and diagnosing genetic conditions, managing patient treatments, and overseeing the program for inherited metabolic diseases at Stanford.

Research Interests

Experience